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Secondary KIT mutations after imatinib failure cluster in exon 13/14 (ATP-binding pocket...

Deterministic view of the source YAML entity. Clinical authority remains with the cited source IDs and reviewer sign-off state.

IDBMA-KIT-EXON13-17-GIST
TypeActionability
Statusreviewed 2026-04-27 | pending_clinical_signoff | actionability review required
DiseasesDIS-GIST
SourcesSRC-CIVIC SRC-NCCN-MELANOMA-2025

Actionability Facts

BiomarkerBIO-KIT
Variantexon 13/14 (ATP-binding) or exon 17/18 (activation loop) secondary mutation post-imatinib
DiseaseDIS-GIST
ESCAT tierIIA
Recommended combinationssunitinib (2L; preferred for exon 13/14 ATP-binding secondaries), regorafenib (3L), ripretinib (4L+; broad activation-loop and ATP-binding coverage)
Contraindicated monotherapyimatinib re-challenge alone (resistant by definition)
Evidence summarySecondary KIT mutations after imatinib failure cluster in exon 13/14 (ATP-binding pocket — V654A, T670I) or exon 17/18 (activation loop — D816, D820, N822, Y823). Sunitinib (Demetri Lancet 2006) covers exon 13/14 secondaries; regorafenib (GRID) provides 3L coverage; ripretinib (INVICTUS) is a switch-control inhibitor active across both classes — preferred 4L+.

Notes

ESCAT IIA. OncoKB Level 1 (per OncoKB therapeutic levels for the approved sequenced TKI flow). Source-gap as DIS-GIST. ctDNA / repeat biopsy can guide TKI selection between sunitinib (ATP-binding) and ripretinib (activation-loop) when secondary genotype is known.

Used By

No reverse references found in the YAML corpus.