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FGFR2 fusion / activating mutation in metastatic urothelial carcinoma: erdafitinib (BLC20...

Deterministic view of the source YAML entity. Clinical authority remains with the cited source IDs and reviewer sign-off state.

IDBMA-FGFR2-MUTATION-UROTHELIAL
TypeActionability
Statusreviewed 2026-04-27 | pending_clinical_signoff | actionability review required
DiseasesDIS-UROTHELIAL
SourcesSRC-CIVIC SRC-EAU-BLADDER-2024 SRC-NCCN-BLADDER-2025

Actionability Facts

BiomarkerBIO-FGFR2
Variantactivating mutation (FGFR2 fusion or kinase-domain mutation)
DiseaseDIS-UROTHELIAL
ESCAT tierIB
Recommended combinationserdafitinib monotherapy (2L+ post-platinum / post-IO)
Evidence summaryFGFR2 fusion / activating mutation in metastatic urothelial carcinoma: erdafitinib (BLC2001, Loriot NEJM 2019 — ORR 40%; THOR phase 3, Loriot NEJM 2023 — OS HR 0.64 vs chemo) is FDA-approved for FGFR2/3-altered locally advanced or metastatic urothelial 2L+. FGFR2 alterations less common than FGFR3 in urothelial (~3% vs ~15%).

Notes

ESCAT IB. OncoKB Level 1. FDA companion diagnostic: therascreen FGFR RGQ RT-PCR (covers FGFR2 fusions and FGFR3 mut/fusions). Detection: RNA-NGS preferred for fusions. Hyperphosphatemia is on-target toxicity requiring dose modification.

Used By

No reverse references found in the YAML corpus.