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FLT3-ITD in relapsed/refractory AML: gilteritinib monotherapy superior to salvage chemo (...

Deterministic view of the source YAML entity. Clinical authority remains with the cited source IDs and reviewer sign-off state.

IDBMA-FLT3-ITD-AML-RR
TypeActionability
Statusreviewed 2026-04-27 | pending_clinical_signoff | actionability review required
DiseasesDIS-AML
SourcesSRC-ADMIRAL-PERL-2019 SRC-CIVIC SRC-ELN-AML-2022 SRC-NCCN-AML-2025

Actionability Facts

BiomarkerBIO-FLT3-ITD
Variantinternal tandem duplication (relapsed/refractory AML)
DiseaseDIS-AML
ESCAT tierIA
Recommended combinationsgilteritinib monotherapy (2L bridge to allo-SCT), gilteritinib + venetoclax + azacitidine (off-label intensification, trial)
Evidence summaryFLT3-ITD in relapsed/refractory AML: gilteritinib monotherapy superior to salvage chemo (ADMIRAL, Perl NEJM 2019 — OS 9.3 vs 5.6 mo, HR 0.64). Gilteritinib is preferred 2L for FLT3-mutant R/R AML and is a bridge to allo-SCT. Quizartinib also active R/R (QuANTUM-R) but FDA label is 1L only (R/R label withdrawn).

Notes

ESCAT IA. OncoKB Level 1. Resistance: F691L gatekeeper, D835 TKD emerge under gilteritinib pressure — see BMA-FLT3-D835-AML-RR and BMA-FLT3-F691L-AML for next-step considerations. Distinguish from BMA-FLT3-ITD-AML which covers 1L.

Used By

No reverse references found in the YAML corpus.